The development of new drugs for genetic diseases
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The genetic diseases of man constitute a unique challenge to the medical scientist. For the past several years our laboratory has been developing new drugs for two of the more common genetic diseases - sickle cell anemia and thalassemia. The status of the development of sodium cyanate as the first chemometallactic agent for the treatment of sickle cell anemia and the development of new iron chelating agents for the treatment of iron overload in patients with thalassemia are discussed.