Browsing by Thesis Advisor "Lorson, Christian L., 1969-"

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  • Gene therapy in mouse models of spinal muscular atrophy : 

    Glascock, Jacqueline J., 1986- (University of Missouri--Columbia, 2013)
    Spinal Muscular Atrophy (SMA), an autosomal recessive neuromuscular disorder, is the leading genetic cause of infant mortality. SMA is caused by the functional, homozygous loss of the Survival Motor Neuron-1 (SMN1) gene ...