Browsing 2009 Dissertations (MU) by Title "Spinal muscular atrophy and the therapeutic application of trans-splicing RNA"
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Spinal muscular atrophy and the therapeutic application of trans-splicing RNA
(University of Missouri--Columbia, 2009)[ACCESS RESTRICTED TO THE UNIVERSITY OF MISSOURI AT REQUEST OF AUTHOR.] Development of RNA modalities to re-direct pathogenic pre-mRNA splicing events is the key to curing monogenic diseases. Improving the efficiency of ...